Two-year results of the ASCEND trial of olipudase alfa adults with chronic acid sphingomyelinase deficiency show parallel improvements in former placebo patients and further improvement in continuing olipudase alfa patients
MOLECULAR GENETICS AND METABOLISM. Bd. 135. H. 2. 2022 S. S126-S127
Erscheinungsjahr: 2022
Publikationstyp: Zeitschriftenaufsatz
| Geprüft: | Bibliothek |
Autoren
Wasserstein, Melissa P. (Autor)
Barbato, Antonio (Autor)
Gallagher, Renata C. (Autor)
Giugliani, Roberto (Autor)
Guelbert, Norberto B. (Autor)
Hennermann, Julia B. (Autor)
Hollak, Carla (Autor)
Ikezoe, Takayuki (Autor)
Lachmann, Robin (Autor)
Lidove, Olivier (Autor)
Mabe, Paulina (Autor)
Mengel, Eugen (Autor)
Scarpa, Maurizio (Autor)
Senates, Ebubekir (Autor)
Tchan, Michel (Autor)
Villarrubia, Jesus (Autor)
Thurberg, Beth L. (Autor)
Yarramaneni, Abhimanyu (Autor)
Rawling, Andreea M. (Autor)
Kim, Yong (Autor)
Kumar, Monica (Autor)
Klassifikation
DDC Sachgruppe:
Medizin
